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Publications du laboratoire Translational Research in Gene Therapy (UMR_S 1089-TARGET)
Vous pouvez consulter et rechercher ici l'ensemble des publications du laboratoire déposées sur HAL. Cette liste de publications est générée automatiquement chaque nuit.
Si au moins un des auteurs de la publication déposée est associé au laboratoire, elle sera intégrée dans cette collection.
Derniers dépôts
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Aurélien Leray, Pierre-Alban Lalys, Juliette Varin, Mohammed Bouzelha, Audrey Bourdon, et al.. Novel chemical tyrosine functionalization of adeno-associated virus improves gene transfer efficiency in liver and retina. Biomedicine and Pharmacotherapy, 2024, 171, pp.116148. ⟨10.1016/j.biopha.2024.116148⟩. ⟨hal-04402650⟩
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Caroline Le Guiner, Xiao Xiao, Thibaut Larcher, Aude Lafoux, Corinne Huchet, et al.. Evaluation of an AAV9-mini-dystrophin gene therapy candidate in a rat model of Duchenne muscular dystrophy. Molecular Therapy - Methods and Clinical Development, 2023, 30, pp.30-47. ⟨10.1016/j.omtm.2023.05.017⟩. ⟨inserm-04240276⟩
Dépôts avec document
68
Dépôts sans document
40
Liens utiles
Politique des revues
Nuage de mots
Animals
Discriminant analysis
Engineering
Gene therapy
Cell–virus interaction
Exon skipping
Accelerometry
Animal model
Analytical ultracentrifugation
Air tamponade
Duchenne
DMD
Human-monocyte-derived dendritic cells
Cone photoreceptors
Intravitreal
Congenital amaurosis
Centronuclear myopathy
Capsid
Childhood blindness
Innate immunity
GC-content
Cell therapy
Click chemistry
Age
Identity
Tolerance
Calcium
Genes
Skeletal muscle
ABCA4
High-throughput sequencing
Capsid assembly
AAV vectors
DMDmdx rat
CMC
Impurities
Capsid thermostability
Clinical trials
Treg
Exercise
Fluid-air exchange
Ectopic expression
Baculovirus
Immune responses
In vivo
GRMD
Immunomodulation
Clinical trial
Infectivity
Immunogenicity
Acute treatment
Intrathymic gene transfer
Homopolymers
Capsid thermal stability
Immunogenicity inflammation gene therapy AAV
Gene Therapy
Gene-therapy
High-throughput technology
GRMD dog
Beta-subunit
Gene transfer
Humoral immunity
Eye surgery
Homologous recombination
Insect cells
Antibodies/immunology/metabolism
Inflammation
Inherited retinal dystrophies
Mice
Quality control
Cerebellum
Dystrophin
Antibody responses
Intra-cerebrospinal fluid injection
AAV vector
Manufacturing
Crigler–Najjar Syndrome
Adenoassociated viral vector
Adeno-associated virus
Identity assay
Vector
Dose study
Gene Transfer
Adenoviridae/immunology
CNS
AAV
Bioconjugates
Assembly-activating protein
Duchenne muscular dystrophy
AUC
CD8 + T lymphocytes
Dynamin 2
Gait assessment
AAP
Homogeneity
Immune response
Baculovirus expression vector
Immunosuppression
Bioorthogonality
B-Lymphocytes/immunology/metabolism