Forelimb loco-regional injection of rAAV8-U7snRNA in GRMD dogs allows dose-dependant dystrophin expression and phenotypic correction
L. Servais
(1, 2)
,
C. Le Guiner
(3)
,
M. Montus
(2)
,
L. Garcia
(4)
,
Y. Fromes
(2)
,
J. Y. Hogrel
(5)
,
P. Carlier
(1)
,
Yan Cherel
(6)
,
P. Moullier
(2)
,
T. Voit
(1)