Intracerebral AAV5-mediated gene transfer in metachromatic leukodystrophy : preclinical study in non human primate
Marie-Anne Colle
(1)
,
F Piguet
(1)
,
L Bertrand
(1)
,
Solène Raoul
(1)
,
Christine Darmon
(1)
,
Laura Jeanneau
(1)
,
M Madi
(1)
,
F Fouquet
(1)
,
Jérôme Amiaud
(1)
,
Yan Cherel
(2)
,
P Moullier
(1)
,
P Aubourg
(1)
,
N Cartier
(1)